Developing therapies for muscle and brain in Duchenne muscular dystrophy
Hybrid event - please contact firstname.lastname@example.org for Teams details.
Drinks reception to follow talk
Duchenne muscular dystrophy is the most common muscular dystrophy affecting children, due to loss of function mutations in the DMD gene. In addition to causing progressive muscle weakness, DMD is also associated with brain comorbidities, which affect nearly 50% of the affected boys.
A number of different therapeutic strategies are under development to improve outcome in DMD, some having received conditional approval in some countries, others at different stages of development.
In this lecture I will provide an overview of the status of some of the most promising therapies under development to improve muscle function in DMD. I will also present the work that our consortium (BIND Consortium, www.bindproject.eu) is doing to consider the implication of genetic therapies to also address the deficiency of the defective gene in brain.
9 November 2023, 16:00 (Thursday, 5th week, Michaelmas 2023)
IMS-Tetsuya Nakamura Building, Roosevelt Dr, Headington OX3 7TY
Prof Francesco Muntoni (UCL Great Ormond Street Hospital)
Medical Sciences Division
Organiser contact email address:
Professor Matthew Wood (University of Oxford)
MDUK Oxford Neuromuscular Centre Seminars
Members of the University only